Title | Single Vector AAV Approach to Genome Editing in Pompe Disease |
Publication Type | Conference Paper |
Year of Publication | 2021 |
Authors | B Arnson, J Wang, D Courtney, S-O Han, S Li, BR Cullen, N Bursac, and D Koeberl |
Conference Name | Molecular Therapy |
Date Published | 01/2021 |